FDA Approval of Nexviazyme (avalglucosidase alfa) For Treatment of Late-Onset Pompe Disease
Dimachkie, MD, FAAN, FANA, Neuromuscular Division Chief at The University of Kansas Health System, discusses Pompe disease, a progressive muscle disor...
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Dimachkie, MD, FAAN, FANA, Neuromuscular Division Chief at The University of Kansas Health System, discusses Pompe disease, a progressive muscle disor...
Richard Furie, Chief, Division of Rheumatology, Northwell Health, and principal investigator in the Saphnelo™ (anifrolumab) clinical trials for the...
Alison Miles, a patient living with Pompe disease, a condition that develops when the body can't make a protein that breaks down a complex sugar, glycog...
Steve Romano, MD, Executive Vice President and Chief Scientific Officer at Mallinckrodt Pharmaceuticals discusses the results of their pivotal Phase 3 ...
Arezou Khosroshahi, MD, Associate Professor of Medicine at Emory University discusses the enrollment of the first patient in Horizon Therapeuti...
Juan Camilo Arjona Ferreira, Chief Medical Officer of Myovant Sciences discusses uterine fibroids and the recent FDA approval of MYFEMBREE® for the tre...
Daniel Catenacci, MD, director of the Gastrointestinal Oncology Program at the University of Chicago, discusses data from Astellas’ Phase 2 FAST study...
Dr. Clare Grace, Chief Patient Officer at Parexel, a leading Clinical Research Organization (CRO) discusses a report titled “Discussions on Diversity” that includes key takeaways...
Jeffrey Stark, MD, Head of Medical Immunology at UCB discusses the results from the BE RADIANT and BE SURE studies, comparing the efficacy and safety of...
Scott Schliebner, SVP and Head of the Center for Rare Diseases at PRA Health Sciences, a global healthcare intelligence partner, discusses the launch of...